Search Result "iduronidase injections"
Intrathecal Enzyme Replacement Therapy for Mucopolysaccharidosis I: Translating Success in Animal Models to Patients
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 946-955
Author(s): Patricia I. Dickson, Agnes H. Chen
Immune Responses to Adenovirus and Adeno-Associated Vectors Used for Gene Therapy of Brain Diseases: The Role of Immunological Synapses in Understanding the Cell Biology of Neuroimmune Interactions
Journal: Current Gene Therapy
Volume: 7 Issue: 5 Year: 2007 Page: 347-360
Author(s): Pedro R. Lowenstein, Ronald J. Mandel, Wei-dong Xiong, Kurt Kroeger, Maria G. Castro
Clinical Development of Cell Therapies to Halt Lysosomal Storage Diseases:Results and Lessons Learned
Journal: Current Gene Therapy
Volume: 22 Issue: 3 Year: 2022 Page: 191-213
Author(s): Valeria Graceffa
Therapies for Neurological Disease in the Mucopolysaccharidoses
Journal: Current Gene Therapy
Volume: 11 Issue: 2 Year: 2011 Page: 132-143
Author(s): Donald S. Anson, Chantelle McIntyre, Sharon Byers
The Significance of Carbohydrate Analyses and the Role of Synthetic substrates in Enzyme Replacement Therapy (ERT) with Special Reference to Mucopolysaccharidosis
Journal: Current Organic Chemistry
Volume: 8 Issue: 6 Year: 2004 Page: 539-555
Author(s): Falguni Dasgupta, R. Irene Masada, Philip L. Alferness, Michael Vellard, William S. Prince
Gene Therapy for Lysosomal Storage Diseases: Progress, Challenges and Future Prospects
Journal: Current Pharmaceutical Design
Volume: 17 Issue: 2 Year: 2011 Page: 2558-2574
Author(s): Sergey S. Seregin, Andrea Amalfitano
Treatment for Lysosomal Storage Disorders
Journal: Current Pharmaceutical Design
Volume: 26 Issue: 40 Year: 2020 Page: 5110-5118
Author(s): Jayesh Sheth,Aadhira Nair
Recent Developments in Therapeutic Approaches for Lysosomal Storage Diseases
Journal: Recent Patents on CNS Drug Discovery (Discontinued)
Volume: 6 Issue: 1 Year: 2011 Page: 1-19
Author(s): Lorena Urbanelli, Alessandro Magini, Alice Polchi, Mario Polidoro, Carla Emiliani
Enzyme Replacement Therapy for Lysosomal Storage Disorders
Journal: Recent Patents on Biomedical Engineering (Discontinued)
Volume: 1 Issue: 2 Year: 2008 Page: 141-147
Author(s): Daniel J. Sayut, Pavan K. R. Kambam, Lianhong Sun
Targeting Brain Disease in Mucopolysaccharidoses
Ebook: Frontiers in Nanomedicine
Volume: 2 Year: 2017
Author(s): Marika Salvalaio,Laura Rigon,Francesca DâAvanzo,Elisa Legnini,Valeria Balmaceda Valdez,Alessandra Zanetti,Rosella Tomanin
Doi: 10.2174/9781681084930117020009