Search Result "Mucopolysaccharidosis IVA"
Mucopolysaccharidosis Type IVA (Morquio A Disease): Clinical Review and Current Treatment: A Special Review
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 931-945
Author(s): S. Tomatsu, A. M. Montano, H. Oikawa, Daniel J. Rowan, M. Smith, L. Barrera, Y. Chinen, M. M. Thacker, W. G. Mackenzie, Y. Suzuki, T. Orii
The Significance of Carbohydrate Analyses and the Role of Synthetic substrates in Enzyme Replacement Therapy (ERT) with Special Reference to Mucopolysaccharidosis
Journal: Current Organic Chemistry
Volume: 8 Issue: 6 Year: 2004 Page: 539-555
Author(s): Falguni Dasgupta, R. Irene Masada, Philip L. Alferness, Michael Vellard, William S. Prince
Effects of Trehalose Administration in Patients withMucopolysaccharidosis Type III
Journal: Current Medicinal Chemistry
Volume: 31 Issue: 20 Year: 2024 Page: 3033-3042
Author(s): Seyed Ahmad Emami,Ali H. Eid
Substrate Reduction Therapies for Mucopolysaccharidoses
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 1 Year: 2011 Page: 1860-1865
Author(s): Joanna Jakobkiewicz-Banecka, Ewa Piotrowska, Magdalena Gabig-Ciminska, Elzbieta Borysiewicz, Monika Slominska-Wojewodzka, Magdalena Narajczyk, Alicja Wegrzyn, Grzegorz Wegrzyn
Treatment of Lysosomal Storage Diseases: Recent Patents and Future Strategies
Journal: Recent Patents on Endocrine, Metabolic & Immune Drug Discovery
Volume: 8 Issue: 1 Year: 2014 Page: 9-25
Author(s): Saida Ortolano,Irene Vieitez,Carmen Navarro,Carlos Spuch
Targeting Brain Disease in Mucopolysaccharidoses
Ebook: Frontiers in Nanomedicine
Volume: 2 Year: 2017
Author(s): Marika Salvalaio,Laura Rigon,Francesca DâAvanzo,Elisa Legnini,Valeria Balmaceda Valdez,Alessandra Zanetti,Rosella Tomanin
Doi: 10.2174/9781681084930117020009
Clinical Development of Cell Therapies to Halt Lysosomal Storage Diseases:Results and Lessons Learned
Journal: Current Gene Therapy
Volume: 22 Issue: 3 Year: 2022 Page: 191-213
Author(s): Valeria Graceffa
Cell-and Gene-based Therapeutic Approaches for Neurological Deficits in Mucopolysaccharidoses
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 884-896
Author(s): Dao Pan
Combined Therapies for Lysosomal Storage Diseases
Journal: Current Molecular Medicine
Volume: 15 Issue: 8 Year: 2015 Page: 746-771
Author(s): M. Gabig-CimiÅska,J. Jakóbkiewicz-Banecka,M. Malinowska,A. Kloska,E. Piotrowska,I. Chmielarz,M. Moskot,A. WÄgrzyn,G. WÄgrzyn
Molecular Pathologies of and Enzyme Replacement Therapies for Lysosomal Diseases
Journal: CNS & Neurological Disorders - Drug Targets
Volume: 5 Issue: 4 Year: 2006 Page: 401-413
Author(s): Hitoshi Sakuraba, Makoto Sawada, Fumiko Matsuzawa, Sei-ichi Aikawa, Yasunori Chiba, Yoshifumi Jigami, Kohji Itoh