Search Result "Maroteaux-Lamy syndrome"
Recent Advances in Treatment Approaches of Mucopolysaccharidosis VI
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 956-972
Author(s): Roberto Giugliani, Clarissa Gutierrez Carvalho, Silvani Herber, Louise Lapagesse de Camargo Pinto
Enzyme Replacement Therapy for Lysosomal Storage Disorders
Journal: Recent Patents on Biomedical Engineering (Discontinued)
Volume: 1 Issue: 2 Year: 2008 Page: 141-147
Author(s): Daniel J. Sayut, Pavan K. R. Kambam, Lianhong Sun
Role of Nanotechnology for Enzyme Replacement Therapy in Lysosomal Diseases. A Focus on Gaucherâs Disease
Journal: Current Medicinal Chemistry
Volume: 23 Issue: 9 Year: 2016 Page: 929-952
Author(s): L. MartÃn-Banderas,M.A. Holgado,M. Durán-Lobato,J.J. Infante,J. Ãlvarez-Fuentes,M. Fernández-Arévalo
Cellular Therapy of Lysosomal Storage Disorders: Current Status and Future Prospects
Journal: Current Pediatric Reviews
Volume: 5 Issue: 3 Year: 2009 Page: 147-159
Author(s): Robert F. Wynn, Matthew Stubbs, Nurdan Ozyilmaz, J. Ed Wraith, Brian Bigger
The Significance of Carbohydrate Analyses and the Role of Synthetic substrates in Enzyme Replacement Therapy (ERT) with Special Reference to Mucopolysaccharidosis
Journal: Current Organic Chemistry
Volume: 8 Issue: 6 Year: 2004 Page: 539-555
Author(s): Falguni Dasgupta, R. Irene Masada, Philip L. Alferness, Michael Vellard, William S. Prince
Mucopolysaccharidosis Type IVA (Morquio A Disease): Clinical Review and Current Treatment: A Special Review
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 931-945
Author(s): S. Tomatsu, A. M. Montano, H. Oikawa, Daniel J. Rowan, M. Smith, L. Barrera, Y. Chinen, M. M. Thacker, W. G. Mackenzie, Y. Suzuki, T. Orii
Therapeutic Suppression of Nonsense Mutation: An Emerging Target in Multiple Diseases and Thrombotic Disorders
Journal: Current Pharmaceutical Design
Volume: 23 Issue: 11 Year: 2017 Page: 1598-1609
Author(s): Md. Asiful Islam,Fahmida Alam,Mohammad Amjad Kamal,Siew Hua Gan,Kah Keng Wong,Teguh Haryo Sasongko
Novel Methods of Genetic Modification of Human Pluripotent Stem Cells
Journal: Recent Patents on Regenerative Medicine
Volume: 5 Issue: 2 Year: 2015 Page: 125-144
Author(s): Maria V. Camarasa
New Advanced Strategies for the Treatment of Lysosomal Diseases Affecting the Central Nervous System
Journal: Current Pharmaceutical Design
Volume: 25 Issue: 17 Year: 2019 Page: 1933-1950
Author(s): Maria R. Gigliobianco,Piera Di Martino,Siyuan Deng,Cristina Casadidio,Roberta Censi
Adeno-associated Viral Vectors for Correction of Inborn Errors of Metabolism: Progressing Towards Clinical Application
Journal: Current Pharmaceutical Design
Volume: 17 Issue: 2 Year: 2011 Page: 2500-2515
Author(s): Frank Jacobs, Lili Wang