Search Result "Pompe disease"
Pompe Disease and Autophagy: Partners in Crime, or Cause and Consequence?
Journal: Current Medicinal Chemistry
Volume: 23 Issue: 21 Year: 2016 Page: 2275-2285
Author(s): M. RodrÃguez-Arribas,J. M. Bravo-San Pedro,R. Gómez-Sánchez,S. M.S. Yakhine-Diop,G. MartÃnez-Chacón,E. Uribe-Carretero,D. C.J. Pinheiro De Castro,I. Casado-Naranjo,A. López de MunaÃn,M. Niso-Santano,J. M. Fuentes,R. A. González-Polo
Reduction of Autophagic Accumulation in Pompe Disease Mouse Model Following Gene Therapy
Journal: Current Gene Therapy
Volume: 19 Issue: 3 Year: 2019 Page: 197-207
Author(s): Angela L. McCall,Sylvia G. Stankov,Gabrielle Cowen,Denise Cloutier,Zizhao Zhang,Lin Yang,Nathalie Clement,Darin J. Falk,Barry J. Byrne
Pompe Disease: From New Views on Pathophysiology to Innovative Therapeutic Strategies
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 902-915
Author(s): Giancarlo Parenti, Generoso Andria
Acid a-Glucosidase Deficiency (Glycogenosis Type II, Pompe Disease)
Journal: Current Molecular Medicine
Volume: 2 Issue: 2 Year: 2002 Page: 145-166
Author(s): Nina Raben, Paul Plotz, Barry J. Byrne
Preclinical Development of New Therapy for Glycogen Storage Diseases
Journal: Current Gene Therapy
Volume: 15 Issue: 4 Year: 2015 Page: 338-347
Author(s): Baodong Sun,Elizabeth D. Brooks,Dwight D. Koeberl
Immunomodulatory Gene Therapy in Lysosomal Storage Disorders
Journal: Current Gene Therapy
Volume: 9 Issue: 6 Year: 2009 Page: 503-510
Author(s): Dwight D. Koeberl, Priya S. Kishnani
Treatment of Lysosomal Storage Diseases: Recent Patents and Future Strategies
Journal: Recent Patents on Endocrine, Metabolic & Immune Drug Discovery
Volume: 8 Issue: 1 Year: 2014 Page: 9-25
Author(s): Saida Ortolano,Irene Vieitez,Carmen Navarro,Carlos Spuch
Feasibility Study for Bedside Production of Recombinant Human Acid α-Glucosidase: Technical and Financial Considerations
Journal: Current Pharmaceutical Biotechnology
Volume: 21 Issue: 6 Year: 2020 Page: 467-479
Author(s): Mohammed H. Aldosari,Marcel den Hartog,Hubertina Ganizada,Martijn J.W. Evers,Enrico Mastrobattista,Huub Schellekens
Lysosomal Storage Diseases: Natural Products Inducing Autophagy
Journal: Current Drug Therapy
Volume: 19 Issue: 5 Year: 2024 Page: 546-560
Author(s):
Late-Onset Glycogen Storage Disease Type 2
Journal: Current Molecular Medicine
Volume: 14 Issue: 8 Year: 2014 Page: 971-978
Author(s): M. Filosto,M.S. Cotelli,V. Vielmi,A. Todeschini,F. Rinaldi,S. Rota,M. Scarpelli,A. Padovani