Search Result "γ-globin"
CNTO 530 Increases Expression of HbA and HbF in Murine Models of β-Thalassemia and Sickle Cell Anemia
Journal: Current Pharmaceutical Biotechnology
Volume: 14 Issue: 2 Year: 2013 Page: 242-248
Author(s): Dorie A. Makropoulos,Ram Achuthanandam,Justin Avery,Krista Wilson,Kerry Brosnan,Andrew Miller,Thomas Nesspor,Denise Chroscinski,Mindi Walker,Devon Egenolf,ChiChi Huang,Peter J. Bugelski
Stem Cell Engineering for the Treatment of Severe Hemoglobinopathies
Journal: Current Molecular Medicine
Volume: 8 Issue: 7 Year: 2008 Page: 690-697
Author(s): Michel Sadelain, Farid Boulad, Leszek Lisowki, Paolo Moi, Isabelle Riviere
Major Challenges for Gene Therapy of Thalassemia and Sickle Cell Disease
Journal: Current Gene Therapy
Volume: 10 Issue: 5 Year: 2010 Page: 404-412
Author(s): Eleni Papanikolaou, Nicholas P. Anagnou
Hemoglobinopathies
Ebook: Omics Technologies for Clinical Diagnosis and Gene Therapy: Medical Applications in Human Genetics
Volume: 1 Year: 2022
Author(s):
Doi: 10.2174/9789815079517122010017
Delivering the "Blueprints" or "DNA Repairing Kits" Instead of Drugs in the Treatment of Congenital Hemoglobinopathies
Journal: Current Organic Chemistry
Volume: 21 Issue: 1 Year: 2017 Page: 74-85
Author(s): Diana Chiru,Cristina Mambet,Lilia Matei,Coralia Bleotu,Simona Ruta,Carmen C. Diaconu
Genetically Modified Hematopoietic Stem Cells for Gene Therapy in Beta-Thalassemia: Power of Viral Vector Towards Clinical Application
Ebook: Recent Advances in Molecular and Translational Medicine: Updates in Precision Medicine
Volume: 1 Year: 2021
Author(s): Kanit Bhukhai,Suparerk Bowornpinyo,Suradej Hongeng
Doi: 10.2174/9789815036756121010011
Advances in Sickle Cell Disease Treatments
Journal: Current Medicinal Chemistry
Volume: 28 Issue: 10 Year: 2021 Page: 2008-2032
Author(s): Aline Renata Pavan,Jean Leandro dos Santos
Preclinical Evaluation of Efficacy and Safety of an Improved Lentiviral Vector for the Treatment of β-Thalassemia and Sickle Cell Disease
Journal: Current Gene Therapy
Volume: 15 Issue: 1 Year: 2015 Page: 64-81
Author(s): Olivier Negre,Cynthia Bartholomae,Yves Beuzard,Marina Cavazzana,Lauryn Christiansen,Celine Courne,Annette Deichmann,Maria Denaro,Edouard de Dreuzy,Mitchell Finer,Raffaele Fronza,Beatrix Gillet-Legrand,Christophe Joubert,Robert Kutner,Philippe Leboulch,Leila Maouche,Anais Paulard,Francis J. Pierciey,Michael Rothe,Byoung Ryu,Manfred Schmidt,Christof von Kalle,Emmanuel Payen,Gabor Veres
RNA as a Drug Target: Recent Patents on the Catalytic Activity of Trans- Splicing Ribozymes Derived from Group I Intron RNA
Journal: Recent Patents on DNA & Gene Sequences (DIscontinued)
Volume: 4 Issue: 1 Year: 2010 Page: 17-28
Author(s): Irudayam Maria Johnson
Regulation of Iron Absorption in Hemoglobinopathies
Journal: Current Molecular Medicine
Volume: 8 Issue: 7 Year: 2008 Page: 646-662
Author(s): Gideon Rechavi, Stefano Rivella