Search Result "efficacy of ERT"
The Significance of Carbohydrate Analyses and the Role of Synthetic substrates in Enzyme Replacement Therapy (ERT) with Special Reference to Mucopolysaccharidosis
Journal: Current Organic Chemistry
Volume: 8 Issue: 6 Year: 2004 Page: 539-555
Author(s): Falguni Dasgupta, R. Irene Masada, Philip L. Alferness, Michael Vellard, William S. Prince
The Role of Ceramide Trihexoside (Globotriaosylceramide) in the Diagnosis and Follow-Up of the Efficacy of Treatment of Fabry Disease: A Review of the Literature
Journal: Cardiovascular & Hematological Agents in Medicinal Chemistry
Volume: 4 Issue: 4 Year: 2006 Page: 289-297
Author(s): Soumeya Bekri, Olivier Lidove, Roland Jaussaud, Bertrand Knebelmann, Frederic Barbey
Pompe Disease: From New Views on Pathophysiology to Innovative Therapeutic Strategies
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 902-915
Author(s): Giancarlo Parenti, Generoso Andria
Bone Remodeling in an Mps-1h Girl after Hematopoietic Stem CellTransplantation along with Enzymatic Replacement Therapy
Journal: Endocrine, Metabolic & Immune Disorders - Drug Targets
Volume: 22 Issue: 14 Year: 2022 Page: 1425-1432
Author(s): Maria Felicia Faienza
Recent Advances in Treatment Approaches of Mucopolysaccharidosis VI
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 956-972
Author(s): Roberto Giugliani, Clarissa Gutierrez Carvalho, Silvani Herber, Louise Lapagesse de Camargo Pinto
Treatment of Lysosomal Storage Diseases: Recent Patents and Future Strategies
Journal: Recent Patents on Endocrine, Metabolic & Immune Drug Discovery
Volume: 8 Issue: 1 Year: 2014 Page: 9-25
Author(s): Saida Ortolano,Irene Vieitez,Carmen Navarro,Carlos Spuch
Enzyme Replacement Therapy for Genetic Disorders Associated withEnzyme Deficiency
Journal: Current Medicinal Chemistry
Volume: 29 Issue: 3 Year: 2022 Page: 489-525
Author(s): Marialaura Marchetti,Serena Faggiano,Andrea Mozzarelli
Can Nanomedicinal Approaches Provide an Edge to the Efficacy ofTyrosine Kinase Inhibitors?
Journal: Current Medicinal Chemistry
Volume: 30 Issue: 13 Year: 2023 Page: 1482-1501
Author(s):
Therapeutic Approaches for Lysosomal Storage Diseases: A Patent Update
Journal: Recent Patents on CNS Drug Discovery (Discontinued)
Volume: 8 Issue: 2 Year: 2013 Page: 91-109
Author(s): Lorena Urbanelli,Krizia Sagini,Mario Polidoro,Alessandro Brozzi,Alessandro Magini,Carla Emiliani
Efficacy of Enzyme Replacement Therapy in Fabry Disease
Journal: Current Medicinal Chemistry - Cardiovascular & Hematological Agents
Volume: 2 Issue: 4 Year: 2004 Page: 277-286
Author(s): F. Barbey, D. Hayoz, U. Widmer, M. Burnier