Search Result "multisystemic lysosomal"

Recent Developments in Therapeutic Approaches for Lysosomal Storage Diseases

Journal: Recent Patents on CNS Drug Discovery (Discontinued)
Volume: 6 Issue: 1 Year: 2011 Page: 1-19
Author(s): Lorena Urbanelli, Alessandro Magini, Alice Polchi, Mario Polidoro, Carla Emiliani

Treatment of Lysosomal Storage Diseases: Recent Patents and Future Strategies

Journal: Recent Patents on Endocrine, Metabolic & Immune Drug Discovery
Volume: 8 Issue: 1 Year: 2014 Page: 9-25
Author(s): Saida Ortolano,Irene Vieitez,Carmen Navarro,Carlos Spuch

Review Article

New Advanced Strategies for the Treatment of Lysosomal Diseases Affecting the Central Nervous System

Journal: Current Pharmaceutical Design
Volume: 25 Issue: 17 Year: 2019 Page: 1933-1950
Author(s): Maria R. Gigliobianco,Piera Di Martino,Siyuan Deng,Cristina Casadidio,Roberta Censi

Mini-Review Article

Clinical Development of Cell Therapies to Halt Lysosomal Storage Diseases:Results and Lessons Learned

Journal: Current Gene Therapy
Volume: 22 Issue: 3 Year: 2022 Page: 191-213
Author(s): Valeria Graceffa

Cellular Therapy of Lysosomal Storage Disorders: Current Status and Future Prospects

Journal: Current Pediatric Reviews
Volume: 5 Issue: 3 Year: 2009 Page: 147-159
Author(s): Robert F. Wynn, Matthew Stubbs, Nurdan Ozyilmaz, J. Ed Wraith, Brian Bigger

Gastroenterological Complications of Anderson-Fabry Disease

Journal: Current Pharmaceutical Design
Volume: 19 Issue: 3 Year: 2013 Page: 6009-6013
Author(s): Piotr Buda, Janusz Ksi azyk, Anna Tylki-Szyma ska

Review Article

Genetics and Gene Therapy in Hunter Disease

Journal: Current Gene Therapy
Volume: 18 Issue: 2 Year: 2018 Page: 90-95
Author(s): S. Sestito,F. Falvo,C. Scozzafava,R. Apa,L. Pensabene,G. Bonapace,M.T. Moricca,D. Concolino

The Fabry Cardiomyopathy - Diagnostic Approach and Current Treatment

Journal: Current Pharmaceutical Design
Volume: 21 Issue: 4 Year: 2015 Page: 473-478
Author(s):

Review Article

Respiratory Complications in the Inborn Errors of Metabolism

Journal: Current Respiratory Medicine Reviews
Volume: 21 Issue: 1 Year: 2025 Page: 93-106
Author(s):

Review Article

Genetics and Gene Therapy of Anderson-Fabry Disease

Journal: Current Gene Therapy
Volume: 18 Issue: 2 Year: 2018 Page: 96-106
Author(s): Irene Simonetta,Antonino Tuttolomondo,Tiziana Di Chiara,Salvatore Miceli,Danai Vogiatzis,Francesca Corpora,Antonio Pinto

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