Search Result "mucopolysaccharidoses (MPS)"
Substrate Reduction Therapies for Mucopolysaccharidoses
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 1 Year: 2011 Page: 1860-1865
Author(s): Joanna Jakobkiewicz-Banecka, Ewa Piotrowska, Magdalena Gabig-Ciminska, Elzbieta Borysiewicz, Monika Slominska-Wojewodzka, Magdalena Narajczyk, Alicja Wegrzyn, Grzegorz Wegrzyn
Cell-and Gene-based Therapeutic Approaches for Neurological Deficits in Mucopolysaccharidoses
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 884-896
Author(s): Dao Pan
Targeting Brain Disease in Mucopolysaccharidoses
Ebook: Frontiers in Nanomedicine
Volume: 2 Year: 2017
Author(s): Marika Salvalaio,Laura Rigon,Francesca DâAvanzo,Elisa Legnini,Valeria Balmaceda Valdez,Alessandra Zanetti,Rosella Tomanin
Doi: 10.2174/9781681084930117020009
Bone Remodeling in an Mps-1h Girl after Hematopoietic Stem CellTransplantation along with Enzymatic Replacement Therapy
Journal: Endocrine, Metabolic & Immune Disorders - Drug Targets
Volume: 22 Issue: 14 Year: 2022 Page: 1425-1432
Author(s): Maria Felicia Faienza
Therapies for Neurological Disease in the Mucopolysaccharidoses
Journal: Current Gene Therapy
Volume: 11 Issue: 2 Year: 2011 Page: 132-143
Author(s): Donald S. Anson, Chantelle McIntyre, Sharon Byers
Help Comes from Unexpected Places: How a Tiny Fairy and a Tropical Fish may help us Model Mucopolysaccharidoses
Journal: Endocrine, Metabolic & Immune Disorders - Drug Targets
Volume: 24 Issue: 16 Year: 2024 Page: 11-11
Author(s):
Mucopolysaccharidosis Type III (Sanfilippo Syndrome): Emerging Treatment Strategies
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 923-930
Author(s): J. de Ruijter, M. J. Valstar, F. A. Wijburg
Mucopolysaccharidosis Type IVA (Morquio A Disease): Clinical Review and Current Treatment: A Special Review
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 931-945
Author(s): S. Tomatsu, A. M. Montano, H. Oikawa, Daniel J. Rowan, M. Smith, L. Barrera, Y. Chinen, M. M. Thacker, W. G. Mackenzie, Y. Suzuki, T. Orii
Intrathecal Enzyme Replacement Therapy for Mucopolysaccharidosis I: Translating Success in Animal Models to Patients
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 946-955
Author(s): Patricia I. Dickson, Agnes H. Chen
Recent Advances in Treatment Approaches of Mucopolysaccharidosis VI
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 956-972
Author(s): Roberto Giugliani, Clarissa Gutierrez Carvalho, Silvani Herber, Louise Lapagesse de Camargo Pinto