Search Result "micro-dystrophin"
Lentiviral Micro-dystrophin Gene Treatment into Late-stage mdx Micefor Duchenne Muscular Dystrophy Disease
Journal: Current Gene Therapy
Volume: 23 Issue: 4 Year: 2023 Page: 304-315
Author(s): Selen Abanuz Eren,Kevser Buse Karadeniz,Raife Dilek Turan,Derya Dilek Kancagi,Sevdican Ustun Yilmaz,Ahmet Tarık Baykal
Adeno-Associated Virus (AAV) Mediated Dystrophin Gene Transfer Studies and Exon Skipping Strategies for Duchenne Muscular Dystrophy (DMD)
Journal: Current Gene Therapy
Volume: 15 Issue: 4 Year: 2015 Page: 395-415
Author(s): Klaudia Kawecka,Michael Theodoulides,Yalin Hasoglu,Susan Jarmin,Hanna Kymalainen,Anita Le-Heron,Linda Popplewell,Alberto Malerba,George Dickson,Takis Athanasopoulos
Gene Replacement Therapies for Duchenne Muscular Dystrophy Using Adeno-Associated Viral Vectors
Journal: Current Gene Therapy
Volume: 12 Issue: 3 Year: 2012 Page: 139-151
Author(s): Jane T. Seto,Julian N. Ramos,Lindsey Muir,Jeffrey S. Chamberlain,Guy L. Odom
Stem Cell-Mediated Exon Skipping of the Dystrophin Gene by the Bystander Effect
Journal: Current Gene Therapy
Volume: 15 Issue: 6 Year: 2015 Page: 563-571
Author(s): Mirella Meregalli,Andrea Farini,Clementina Sitzia,Cyriaque Beley,Paola Razini,Letizia Cassinelli,Federica Colleoni,Paola Frattini,Nadia Santo,Elisabetta Galbiati,Davide Prosperi,Alessandro Tavelli,Marzia Belicchi,Luis Garcia,Yvan Torrente
Splice Modification to Restore Functional Dystrophin Synthesis in Duchenne Muscular Dystrophy
Journal: Current Pharmaceutical Design
Volume: 16 Issue: 8 Year: 2010 Page: 988-1001
Author(s): Steve. D. Wilton, Susan Fletcher
Proteomics of the Dystrophin-glycoprotein Complex and Dystrophinopathy
Journal: Current Protein & Peptide Science
Volume: 14 Issue: 8 Year: 2013 Page: 680-697
Author(s): Ashling Holland,Steven Carberry,Kay Ohlendieck
Developing Effective Therapy for Duchenne Muscular Dystrophy (DMD): Challenges and Promises
Journal: Current Chemical Biology
Volume: 8 Issue: 3 Year: 2014 Page: 117-131
Author(s): Trinath Ghosh,Ujjal Ghosh,Gargi Ghosh,Dabasish Malik,Shankhamala Bose,Utpal Basu
Therapeutic DNA Delivery to Skeletal Muscle
Journal: Current Genomics
Volume: 7 Issue: 3 Year: 2006 Page: 179-190
Author(s): Anita Quigley, Kym Lowes, Andrew J. Kornberg, Mark J. Cook, Robert Kapsa
Muscular Dystrophies: Histology, Immunohistochemistry, Molecular Genetics and Management
Journal: Current Pharmaceutical Design
Volume: 16 Issue: 8 Year: 2010 Page: 978-987
Author(s): Costanza Lamperti, Maurizio Moggio
Cell Penetrating Peptide Delivery of Splice Directing Oligonucleotides as a Treatment for Duchenne Muscular Dystrophy
Journal: Current Pharmaceutical Design
Volume: 19 Issue: 1 Year: 2013 Page: 2948-2962
Author(s): Corinne A. Betts, Matthew J.A. Wood