Search Result "Alpha-l-iduronidase"
Bone Remodeling in an Mps-1h Girl after Hematopoietic Stem CellTransplantation along with Enzymatic Replacement Therapy
Journal: Endocrine, Metabolic & Immune Disorders - Drug Targets
Volume: 22 Issue: 14 Year: 2022 Page: 1425-1432
Author(s): Maria Felicia Faienza
Chloramphenicol Enhances IDUA Activity on Fibroblasts from Mucopolysaccharidosis I Patients
Journal: Current Pharmaceutical Biotechnology
Volume: 14 Issue: 2 Year: 2013 Page: 194-198
Author(s): Fabiana Quoos Mayer,Osvaldo Alfonso Artigalas,Valeska Lizzi Lagranha,Guilherme Baldo,Ida Vanessa Schwartz,Ursula Matte,Roberto Giugliani
Intrathecal Enzyme Replacement Therapy for Mucopolysaccharidosis I: Translating Success in Animal Models to Patients
Journal: Current Pharmaceutical Biotechnology
Volume: 12 Issue: 6 Year: 2011 Page: 946-955
Author(s): Patricia I. Dickson, Agnes H. Chen
Enzyme Replacement Therapy for Lysosomal Storage Disorders
Journal: Recent Patents on Biomedical Engineering (Discontinued)
Volume: 1 Issue: 2 Year: 2008 Page: 141-147
Author(s): Daniel J. Sayut, Pavan K. R. Kambam, Lianhong Sun
Clinical Development of Cell Therapies to Halt Lysosomal Storage Diseases:Results and Lessons Learned
Journal: Current Gene Therapy
Volume: 22 Issue: 3 Year: 2022 Page: 191-213
Author(s): Valeria Graceffa
Gene Therapy for Lysosomal Storage Diseases: Progress, Challenges and Future Prospects
Journal: Current Pharmaceutical Design
Volume: 17 Issue: 2 Year: 2011 Page: 2558-2574
Author(s): Sergey S. Seregin, Andrea Amalfitano
Therapies for Neurological Disease in the Mucopolysaccharidoses
Journal: Current Gene Therapy
Volume: 11 Issue: 2 Year: 2011 Page: 132-143
Author(s): Donald S. Anson, Chantelle McIntyre, Sharon Byers
Therapeutic Suppression of Nonsense Mutation: An Emerging Target in Multiple Diseases and Thrombotic Disorders
Journal: Current Pharmaceutical Design
Volume: 23 Issue: 11 Year: 2017 Page: 1598-1609
Author(s): Md. Asiful Islam,Fahmida Alam,Mohammad Amjad Kamal,Siew Hua Gan,Kah Keng Wong,Teguh Haryo Sasongko
Cell and Gene-Based Therapies for the Lysosomal Storage Diseases
Journal: Current Gene Therapy
Volume: 6 Issue: 2 Year: 2006 Page: 227-241
Author(s): Bradley L. Hodges, Seng H. Cheng
Pharmacological Suppression of Premature Stop Mutations that Cause Genetic Diseases
Journal: Current Pharmacogenomics
Volume: 3 Issue: 4 Year: 2005 Page: 259-269
Author(s): K. M. Keeling, D. M. Bedwell