Search Result "exon-skipping"
Personalised Genetic Intervention for Duchenne Muscular Dystrophy: Antisense Oligomers and Exon Skipping
Journal: Current Molecular Pharmacology
Volume: 2 Issue: 1 Year: 2009 Page: 110-121
Author(s): Chalermchai Mitrpant, Sue Fletcher, Steve D. Wilton
Antisense Oligonucleotide-Mediated Exon Skipping for Duchenne Muscular Dystrophy: Progress and Challenges
Journal: Current Gene Therapy
Volume: 12 Issue: 3 Year: 2012 Page: 152-160
Author(s): Virginia Arechavala-Gomeza,Karen Anthony,Jennifer Morgan,Francesco Muntoni
Repurposing Pathogenic Variants of DMD Gene and its Isoforms for DMD Exon Skipping Intervention
Journal: Current Genomics
Volume: 20 Issue: 7 Year: 2019 Page: 519-530
Author(s): Rahul Tyagi,Sumit Kumar,Ashwin Dalal,Faruq Mohammed,Manju Mohanty,Paramvir Kaur,Akshay Anand
The Treatment of a New Entity in Advanced Non-small Cell LungCancer: MET Exon 14 Skipping Mutation
Journal: Current Medicinal Chemistry
Volume: 31 Issue: 21 Year: 2024 Page: 3043-3056
Author(s): Luigi Della Gravara
Adeno-Associated Virus (AAV) Mediated Dystrophin Gene Transfer Studies and Exon Skipping Strategies for Duchenne Muscular Dystrophy (DMD)
Journal: Current Gene Therapy
Volume: 15 Issue: 4 Year: 2015 Page: 395-415
Author(s): Klaudia Kawecka,Michael Theodoulides,Yalin Hasoglu,Susan Jarmin,Hanna Kymalainen,Anita Le-Heron,Linda Popplewell,Alberto Malerba,George Dickson,Takis Athanasopoulos
Stem Cell-Mediated Exon Skipping of the Dystrophin Gene by the Bystander Effect
Journal: Current Gene Therapy
Volume: 15 Issue: 6 Year: 2015 Page: 563-571
Author(s): Mirella Meregalli,Andrea Farini,Clementina Sitzia,Cyriaque Beley,Paola Razini,Letizia Cassinelli,Federica Colleoni,Paola Frattini,Nadia Santo,Elisabetta Galbiati,Davide Prosperi,Alessandro Tavelli,Marzia Belicchi,Luis Garcia,Yvan Torrente
Splice Modification to Restore Functional Dystrophin Synthesis in Duchenne Muscular Dystrophy
Journal: Current Pharmaceutical Design
Volume: 16 Issue: 8 Year: 2010 Page: 988-1001
Author(s): Steve. D. Wilton, Susan Fletcher
Developing Effective Therapy for Duchenne Muscular Dystrophy (DMD): Challenges and Promises
Journal: Current Chemical Biology
Volume: 8 Issue: 3 Year: 2014 Page: 117-131
Author(s): Trinath Ghosh,Ujjal Ghosh,Gargi Ghosh,Dabasish Malik,Shankhamala Bose,Utpal Basu
Antisense Therapy for Cardiovascular Diseases
Journal: Current Pharmaceutical Design
Volume: 21 Issue: 30 Year: 2015 Page: 4417-4426
Author(s): M. Ian Phillips,Jessica Costales,Robert J. Lee,Edilamar Oliveira,Andrew B. Burns
Limb-girdle Muscular Dystrophy and Therapy: Insights into Cell and Gene-based Approaches
Journal: Current Gene Therapy
Volume: 19 Issue: 6 Year: 2019 Page: 386-394
Author(s): Forough Taheri,Eskandar Taghizadeh,Mohammad J.R. Pour,Daryoush Rostami,Pedram G. Renani,Azam Rastgar-Moghadam,Seyed M.G. Hayat