Search Result "ataluren"
Duchenne Muscular Dystrophy Management and Treatment Access Challenges:Case Report
Journal: New Emirates Medical Journal
Volume: 4 Issue: 1 Year: 2023 Page: 1-5
Author(s): Tarek I. El-Azzabi
Therapeutic Suppression of Nonsense Mutation: An Emerging Target in Multiple Diseases and Thrombotic Disorders
Journal: Current Pharmaceutical Design
Volume: 23 Issue: 11 Year: 2017 Page: 1598-1609
Author(s): Md. Asiful Islam,Fahmida Alam,Mohammad Amjad Kamal,Siew Hua Gan,Kah Keng Wong,Teguh Haryo Sasongko
Meet Our Editorial Board Member
Journal: Current Drug Discovery Technologies
Volume: 16 Issue: 4 Year: 2019 Page: 317-317
Author(s): Marco Tutone
A Review on Novel Synthesis Approaches and Biological Activities of 1,2,4-Oxadiazole and 1,3,4-Oxadiazole Tailored Compounds
Journal: Current Organic Synthesis
Volume: 19 Issue: 6 Year: 2022 Page: 731-747
Author(s): Prabhat Kumar Upadhyay
The Development of Drug Therapies for Frontotemporal Dementia Caused by Progranulin Mutations
Ebook: Frontiers in Clinical Drug Research - Alzheimer Disorders
Volume: 3 Year: 2015
Author(s): Louis De Muynck,Philip Van Damme
Doi: 10.2174/9781681080680115030007
Adeno-Associated Virus (AAV) Mediated Dystrophin Gene Transfer Studies and Exon Skipping Strategies for Duchenne Muscular Dystrophy (DMD)
Journal: Current Gene Therapy
Volume: 15 Issue: 4 Year: 2015 Page: 395-415
Author(s): Klaudia Kawecka,Michael Theodoulides,Yalin Hasoglu,Susan Jarmin,Hanna Kymalainen,Anita Le-Heron,Linda Popplewell,Alberto Malerba,George Dickson,Takis Athanasopoulos
Editorial (Hot Topic:Cystic Fibrosis: CFTR Modulators and their Mechanism of Action)
Journal: Current Pharmaceutical Design
Volume: 19 Issue: 1 Year: 2013 Page: 3474-3475
Author(s): Erika Nieddu
New Therapies in Cystic Fibrosis
Journal: Current Pharmaceutical Design
Volume: 18 Issue: 5 Year: 2012 Page: 614-627
Author(s): Felix Ratjen, Hartmut Grasemann
Personalized Drug Therapy in Cystic Fibrosis: From Fiction to Reality
Journal: Current Drug Targets
Volume: 16 Issue: 9 Year: 2015 Page: 1007-1017
Author(s): Fernando Augusto de Lima Marson,Carmen Silvia Bertuzzo,Jose Dirceu Ribeiro
Triazole and Oxadiazole Containing Natural Products: A Review
Journal: The Natural Products Journal
Volume: 4 Issue: 2 Year: 2014 Page: 115-130
Author(s): Vinod Kumar,Kamalneet Kaur