摘要
虽然腺相关病毒载体的研究由来已久,但是其作为一种重要可行的基因治疗策略已被推到注意中心只在最近几年。由于这些载体的优良特性,它们的潜力已精心利用在多种神经系统疾病的治疗。本文在扼要介绍的腺相关病毒载体治疗进展的治疗帕金森病的研究各种动物模型实验和临床试验针对基因治疗的腺相关病毒载体的出现。此外,在审查研究的年代学分析使得它更容易理解的挑战和预言未来的前景在这一领域的治疗药物。
关键词: 腺相关病毒,腺相关病毒,帕金森氏病的基因治疗。
Current Gene Therapy
Title:Therapeutic Value of Adeno Associated Virus as a Gene Therapy Vector for Parkinson's Disease – A Focused Review
Volume: 16 Issue: 4
Author(s): Aastha Singh, Dwaipayan Sen
Affiliation:
关键词: 腺相关病毒,腺相关病毒,帕金森氏病的基因治疗。
摘要: Although adeno-associated viral vectors have been studied for a long time, its importance as a viable gene therapy strategy has been thrusted into the limelight only in the recent years. Due to the admirable characteristics of these vectors, their potential has been thoughtfully utilized in the treatment of several neurodegenerative diseases. This mini-review focuses at recapitulating the therapeutic advances of adeno-associated viral vectors in the treatment of Parkinson’s disease by studying the various animal model experiments and clinical trials conducted since the advent of adeno-associated viral vector - based gene therapy. Additionally, the chronological analysis of the studies in the review makes it easier to understand the challenges and foretell the future prospects in this field of therapeutics.
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Aastha Singh, Dwaipayan Sen , Therapeutic Value of Adeno Associated Virus as a Gene Therapy Vector for Parkinson's Disease – A Focused Review, Current Gene Therapy 2016; 16 (4) . https://dx.doi.org/10.2174/1566523216666160729113558
DOI https://dx.doi.org/10.2174/1566523216666160729113558 |
Print ISSN 1566-5232 |
Publisher Name Bentham Science Publisher |
Online ISSN 1875-5631 |
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